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== Orphan Patient == ...ient suffering from a rare disease or condition, often referred to as an [[orphan disease]].

'''Orphan drug''' ...t a rare medical condition, the condition itself being referred to as an [[orphan disease]].

...s]]. It is a database dedicated to information on rare diseases and orphan drugs (available in 40 countries). ...is a combination of "orphan" and "net", referring to its focus on [[orphan drugs]] and its nature as an online network.

...s significant contributions to the field of [[rare diseases]] and [[orphan drugs]]. ...eases. His work led to the development of two significant [[FDA]]-approved drugs, Aldurazyme and Naglazyme, which treat [[Mucopolysaccharidosis I (MPS I)]]

...tion. The exact definition of a rare disease varies, but in general, it is a disease that affects fewer than 200,000 people in the United States at any ...iseases" comes from the fact that these diseases are not common. The term "orphan diseases" comes from the fact that these diseases are often neglected by th

...'' (pronounced: noo-MOR-fan) is a brand name for the drug [[Oxymorphone]], a powerful semi-synthetic opioid analgesic first developed in Germany circa 1 ...tus as a derivative of the opium poppy, which is often referred to as the "orphan" of the plant world due to its solitary growth habit.

...des certain benefits to the drug developer to encourage the development of drugs for the small market of individuals with these conditions. Orphan drug designation: /ˈɔːrfən drʌg ˌdɛzɪɡˈneɪʃən/

...[enzyme replacement therapy]] used for the treatment of [[Pompe disease]], a rare genetic disorder. ...osidase. "Alfa" is a common suffix used in pharmaceutical naming to denote a product of recombinant DNA technology.

...maceutical companies with certain financial benefits for developing orphan drugs that are safe and effective {{dictionary-stub}} [[Category:Dictionary of me

'''Dextrorphan''' (''pronunciation: dex-tro-or-fan'') is a psychoactive drug of the morphinan chemical class which acts as an antituss ...intended for human use. The "dextro" prefix is used in chemistry to denote a molecule that rotates plane-polarized light to the right.

...improve the safety or effectiveness of treating, diagnosing, or preventing a serious condition. This designation is intended to direct overall attention ...riority", meaning precedence in order or importance, and "review", meaning a formal assessment or examination.

...ntuzumab mafodotin''' (pronunciation: den-in-tuz-oo-mab maf-oh-doe-tin) is a [[monoclonal antibody]] designed for the treatment of [[cancer]]. ...oad, monomethyl auristatin F (MMAF), which is attached to the antibody via a linker.

...tuzumab Ozogamicin''' (pronounced as gem-too-zoo-mab oh-zoh-ga-mye-sin) is a [[monoclonal antibody]] used in the treatment of [[acute myeloid leukemia]] ...ing to gemtuzumab, the humanized monoclonal antibody, and '''tuzumab''' is a stem used for humanized antibodies. '''Ozogamicin''' refers to the cytotoxi

...it the [[ROR1]] (Receptor tyrosine kinase-like Orphan Receptor 1) protein, a type of [[oncoprotein]] that is overexpressed in many different types of [[ ...Regenerative Medicine), which funded the initial research, and "tuzumab", a common suffix for monoclonal antibodies.

...dustry]] to describe a new drug substance or an old drug substance used in a new manner for which approval for marketing in the United States has not ye ...mine the facts so as to establish the truth. The term "new drug" refers to a substance that has not been approved for use in the market.

'''Medical terminology''' is a language used to precisely describe the human body including its components * '''[[Prefixes]]''': Added to the beginning of a word to modify its meaning, such as location, time, or status.

...etic lenses: conventional eyeglasses || {{#cargo_store:_table=dmesuppliers|A=43751|Provider_ID=17528077|Accepts_medicare=Yes|Business_name=Dr Burt S Esc ...glucose monitors/supplies (mail order), ostomy supplies, immunosuppressive drugs, parenteral equipment and/or supplies, nebulizer equipment and/or supplies,

...proteins occurring on red blood cells; the four classification groups are A, AB, B, and O * [[ACE inhibitor]] - a drug typically used to treat high blood pressure (Angiotensin-Converting